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Business
New tumor cases show common gene therapy tool can come with risk
The FDA launches an investigation into Novartis' Zolgensma gene therapy following reports of new tumor cases.
Gene Therapy
29 trends tracked about this subject — the full history, oldest to newest below.
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Health
Epileptic seizures nearly vanish after people receive experimental gene therapy in their brains
Experimental brain gene therapy cuts drug-resistant epilepsy seizures by over ninety percent in human trials.
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Business
Seven new tumor cases reported among patients on Novartis’ Zolgensma gene therapy
1 news sources are covering this Business story right now — PULSE is tracking how fast it spreads.
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Business
Novartis cites cases of previously unknown tumors possibly tied to its SMA gene therapy
Novartis reports cases of tumors in children following treatment with its spinal muscular atrophy gene therapy, Zolgensma.
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Technology
An AI Agent Injected Drugs Into a Live Mouse’s Brain
An autonomous AI agent has performed a gene therapy brain injection on a live mouse after a refusal by an earlier model.
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Science
Gene therapy that led to boy’s death had limited efficacy
Recent coverage examines a fatal gene-editing trial in China that showed limited efficacy alongside severe safety concerns.
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Business
FDA offers new details on quicker approval pathway for personalized gene therapies
12 news sources are covering this Business story right now — PULSE is tracking how fast it spreads.
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Technology
Hugging Face’s New AI Biology Model Lets You Chat With DNA
5 news sources are covering this Technology story right now — PULSE is tracking how fast it spreads.
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Health
Transcriptomic reprogramming screen identifies SRSF1 as a regulator of aging
Recent scientific coverage reveals that delivering the SRSF1 gene extends median lifespan and reverses aging indicators in aged mice.
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Health
Partial Vision Restored in Some Blind Patients With New Experimental Treatment
Recent coverage highlights experimental optogenetic therapies and specialized goggles restoring partial vision in blind adults.
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Health
NEWSLETTER: Blindness treatment based on Nobel-winning research shows promise
Swiss gene therapy for blindness, rooted in Nobel-winning research, shows further encouraging progress according to recent reports.
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Health
Optogenetic Therapy for Restoring Aspects of Visual Function
Recent scientific findings detail the use of optogenetic therapy and special goggles to restore limited vision in blind patients.
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Health
Gene therapy can partly restore sight in blind people, researchers reveal
Gene therapy linked to Nobel-winning research shows promise in restoring limited sight to blind patients.
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Health
A one-time treatment may fix damaged adult retinas
5 news sources are covering this Health story right now — PULSE is tracking how fast it spreads.
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Business
FDA approves a new gene therapy for Sanfilippo syndrome, an ultra-rare disease
FDA approves Ultragenyx's gene therapy Fayuvi for Sanfilippo syndrome at a price of $3.95 million.
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Health
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‘Curved Air’ Review: A Mutation’s Painful Legacy
Medical advancements in gene therapy are transforming the lives of sickle cell patients, highlighted by new treatments and cultural reflections.
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Business
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Regenxbio gene therapy refiling plan derailed by FDA hold over spine MRI findings
2 news sources are covering this Business story right now — PULSE is tracking how fast it spreads.
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Business
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FDA pauses Regenxbio gene therapy trial again due to safety concerns
The FDA has placed a clinical hold on Regenxbio's gene therapy for Hunter Syndrome following safety concerns related to spine MRI findings.
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Health
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Exclusive: Third death in China's popular but opaque trials revealed, this time in CAR-T
Coverage reveals a third death in opaque Chinese clinical trials involving CAR-T therapy, intensifying global scrutiny.
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Health
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The ethical perils of gene therapy
The death of a child in a gene editing trial exposes the ethical perils and limits of scientific advancement.
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Health
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6-year-old girl dies after parents paid $860K for experimental therapy that ‘shouldn’t have gone to trial’
3 news sources are covering this Health story right now — PULSE is tracking how fast it spreads.
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Health
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Targeting Allele-Specific Faulty MRNA In SCNA2 Mutation Patients
Personalized gene therapy using bespoke ASOs has enabled a teen with SCN2A-related epileptic encephalopathy to walk independently for the first time.
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Health
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$160 million ‘moonshot’ backs Boston effort to revolutionize rare disease treatment
A $160 million non-profit initiative in Boston aims to revolutionize the development of genetic medicines for rare and ultra-rare diseases.
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Business
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FDA’s top gene therapy regulator is leaving his role
11 news sources are covering this Business story right now — PULSE is tracking how fast it spreads.
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Health
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Louisiana Notches a Sickle Cell First
8 news sources are covering this Health story right now — PULSE is tracking how fast it spreads.
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Health
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Scientists begin first trial to reverse human aging
Researchers have initiated the first human clinical trial focused on reversing cellular aging through experimental gene therapy.
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Business
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Exclusive | FDA Gives Third Rare-Disease Drug Another Shot, Regenxbio Says
The FDA is allowing Regenxbio to resubmit its gene therapy for Hunter syndrome, marking a reversal of a previous rejection.
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Health
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'I've never been this good'
A lupus treatment borrowed from cancer therapy is putting patients into remission—with one calling it life-changing.
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Health
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What’s the Future of Gene Editing?
The gene editing landscape is expanding rapidly through next-generation CRISPR tools and significant projected market growth through 2028.